NHS to give children with rare fatal genetic disease 'world's most expensive drug' - The Mirror

The gene therapy treatment is used to treat metachromatic leukodystrophy (MLD), which causes severe damage to a child's nervous system and organs.
https://www.google.com/url?rct=j&sa=t&url=https://www.mirror.co.uk/news/uk-news/nhs-give-children-rare-fatal-26140020&ct=ga&cd=CAIyGmEyNDJjNTAxZWU3OTQyNzI6Y29tOmVuOlVT&usg=AFQjCNEvGfW2-7spVdfUUwYcLRHioG9Rqw